Rare diseases
541 results
1 - 100Interventions for the treatment of Paget's disease of the vulva: Cochrane systematic review
Interventions for mucous membrane pemphigoid and epidermolysis bullosa acquisita
Chemotherapy for malignant germ cell ovarian cancer in adult patients with early stage, advanced and recurrent disease
Chemotherapy and/or radiotherapy in combination with surgery for ovarian carcinosarcoma
Vaccines for preventing plague: Cochrane systematic review
Immune tolerance induction for treating inhibitors in people with congenital haemophilia A or B
Calcitonin testing for detection of medullary thyroid cancer in people with thyroid nodules
Medical treatment for botulism: Cochrane systematic review
Natalizumab for induction of remission in Crohn's disease
Pneumococcal vaccines for preventing pneumonia in chronic obstructive pulmonary disease
Cemented, cementless or hybrid fixation options in total knee arthroplasty for osteoarthritis and other non-traumatic diseases: Cochrane systematic review
Drug treatment for myotonia
Sulfasalazine for ankylosing spondylitis
Natalizumab for relapsing remitting multiple sclerosis: Cochrane systematic review
Role of chemotherapy additional to high-dose methotrexate for primary central nervous system lymphoma (PCNSL): Cochrane systematic review
Notification and support for people exposed to the risk of Creutzfeldt‐Jakob disease (CJD) (or other prion diseases) through medical treatment (iatrogenically)
Enzyme replacement and substrate reduction therapy for Gaucher disease
Physical training for McArdle disease: Cochrane systematic review
Metformin for preventing the progression of chronic kidney disease
Azathioprine or 6‐mercaptopurine for induction of remission in Crohn's disease
Topical tacrolimus for atopic dermatitis
Antiviral agents for treatment of herpes simplex virus infection in neonates: Cochrane systematic review
Antibiotics for syphilis diagnosed during pregnancy
Methotrexate for ankylosing spondylitis
Pharmacological treatments for Friedreich ataxia
Surgery for Dupuytren's contracture of the fingers
Enzyme replacement therapy for late‐onset Pompe disease
Pentoxifylline for alcoholic hepatitis
Enzyme replacement therapy for Anderson‐Fabry disease
Abatacept for rheumatoid arthritis
Pain management for rheumatoid arthritis and cardiovascular or renal comorbidity
Treadmill training for patients with Parkinson's disease
Prazosin for Raynaud's phenomenon in progressive systemic sclerosis
The impact of surgical therapies for inflammatory bowel disease on female fertility
Colchicine for primary biliary cirrhosis
Nutritional supplementation for nonalcohol‐related fatty liver disease: a network meta‐analysis
Interventions for atypical haemolytic uraemic syndrome
Inhaled corticosteroids versus long‐acting beta2‐agonists for chronic obstructive pulmonary disease
Oral adsorbents for preventing or delaying the progression of chronic kidney disease
Pembrolizumab monotherapy versus chemotherapy for treatment of advanced urothelial carcinoma with disease progression during or following platinum‐containing chemotherapy. A Cochrane Rapid Review
Interventions for hyperthyroidism pre-pregnancy and during pregnancy: Cochrane systematic review
Vaccines for preventing pneumococcal infection in adults
Bisphosphonates for Paget's disease of bone in adults
Immunosuppressive treatment for non‐systemic vasculitic neuropathy
Venous thromboembolism prophylaxis for women at risk during pregnancy and the early postnatal period
Surgical interventions for early squamous cell carcinoma of the vulva: Cochrane systematic review
Non‐corticosteroid immunosuppressive medications for steroid‐sensitive nephrotic syndrome in children
Cromolyn sodium for the prevention of chronic lung disease in preterm infants
Glucocorticosteroids for primary sclerosing cholangitis: Cochrane systematic review
Etanercept for the treatment of rheumatoid arthritis: Cochrane systematic review
Treatment for familial amyotrophic lateral sclerosis/motor neuron disease
Interventions for managing oral ulcers in Behçet's disease
Colony‐stimulating factors for prevention and treatment of infectious complications in patients with acute myelogenous leukemia
Vaginal chlorhexidine during labour to prevent early-onset neonatal group B streptococcal infection: Cochrane systematic review
Calcium channel blockers for people with chronic kidney disease requiring dialysis
Acetylcysteine and carbocysteine for acute upper and lower respiratory tract infections in paediatric patients without chronic broncho‐pulmonary disease
Adjuvant radiotherapy and/or chemotherapy after surgery for uterine carcinosarcoma
Interventions for toxic epidermal necrolysis
Fludrocortisone for orthostatic hypotension
Febuxostat for treating chronic gout
Thyroid surgery for Graves’ disease and Graves’ ophthalmopathy: Cochrane systematic review
Interferon for acute hepatitis C: Cochrane systematic review
Interventions for treating intrahepatic cholestasis in people with sickle cell disease
Surgery for chronic arthropathy in people with haemophilia
Antiplatelet drugs for polycythaemia vera and essential thrombocythaemia
Non‐steroidal anti‐inflammatory drugs (NSAIDs) for axial spondyloarthritis (ankylosing spondylitis and non‐radiographic axial spondyloarthritis)
Surgical removal versus retention for the management of asymptomatic disease‐free impacted wisdom teeth
Statins for acute coronary syndrome
Shouldice technique versus other open techniques for inguinal hernia repair: Cochrane systematic review
Treatment of infantile spasms
Hormonal versus non‐hormonal contraceptives in women with diabetes mellitus type 1 and 2
Interventions for cutaneous Bowen's disease
Conjugate Haemophilus influenzae type b vaccines for sickle cell disease
Interventions for prophylaxis of hepatic veno-occlusive disease in people undergoing haematopoietic stem cell transplantation: Cochrane systematic review
Chemotherapy for brain metastases from small cell lung cancer: Cochrane systematic review
Lipid‐lowering agents for nephrotic syndrome
Effectiveness of different treatment modalities for the management of adult‐onset granulosa cell tumours of the ovary (primary and recurrent)
Stem cell therapy for chronic ischaemic heart disease and congestive heart failure
Anti‐vascular endothelial growth factor biosimilars for neovascular age‐related macular degeneration
Bezafibrate for primary biliary cirrhosis: Cochrane systematic review
Singing for children and adults with bronchiectasis: Cochrane systematic review
Topical and oral steroids for otitis media with effusion (OME) in children
Pharmacological interventions for painful sickle cell vaso‐occlusive crises in adults
Immunosuppressive agents for treating IgA nephropathy
Exercise programmes for ankylosing spondylitis
Information provision for people with multiple sclerosis
Interferon after surgery for women with advanced (Stage II‐IV) epithelial ovarian cancer
Intramuscular penicillin for the prevention of early onset group B streptococcal infection in newborn infants
Treatment for POEMS (polyneuropathy, organomegaly, endocrinopathy, M‐protein, and skin changes) syndrome